Gene Therapy for Hemophilia: A Step Closer to Reality
نویسندگان
چکیده
منابع مشابه
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Heterogeneous loss of function mutations at F8 and F9 genes causes X-linked recessive bleeding disorders, hemophilia A (HA) and hemophilia B (HB), respectively. HA is clinically indistinguishable from HB and accounts for more than 80% of hemophilia cases; the former affects 1/5000 and the latter 1/25000 male births worldwide. In Iran, it is estimated that around 4300 HA and 900 HB patients are ...
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ژورنال
عنوان ژورنال: Molecular Therapy
سال: 2000
ISSN: 1525-0016
DOI: 10.1006/mthe.2000.0048